Tag: rare diseases

STAT+: New tumor cases show common gene therapy tool can come with risk

Health & well-being news
For two decades, researchers debated whether adeno-associated viruses, the small viruses used to deliver new genes into thousands of...

STAT+: Servier’s $1.55 billion muscular dystrophy drug fails first major test

Health & well-being news
The French pharma Servier said Tuesday that an experimental drug it purchased in June for $1.55 billion in cash,...